Recruiting
Phase 3
Sarcoma,Soft Tissue
Intensity Therapeutics, Inc. · started 2024-06-28
📍 California · Connecticut · Michigan · Nebraska · North Carolina · Ohio · Pennsylvania
NCT06263231 on ClinicalTrials.gov ↗
Recruiting
Phase 3
CLL / SLL, CLL (Chronic Lymphocytic Leukemia), CLL, Refractory, CLL, Relapsed
Newave Pharmaceutical Inc · started 2026-04-23
📍 Illinois · Maryland · Nevada · Ohio · Pennsylvania · Washington
NCT07342478 on ClinicalTrials.gov ↗
Recruiting
Phase 3
Alpha 1 Antitrypsin Deficiency
Grifols Therapeutics LLC · started 2026-05-05
📍 Alabama · Arizona · California · Florida · Minnesota · Ohio · South Carolina · Texas
NCT07555483 on ClinicalTrials.gov ↗
Active
Phase 1/Phase 2
Metastatic Microsatellite-stable Colorectal Cancer
MedImmune LLC · started 2019-09-13
📍 California · Michigan · Nevada · New York · Ohio · Rhode Island · Tennessee · Texas
NCT04068610 on ClinicalTrials.gov ↗
Recruiting
Phase 2
Respiratory Syncytial Virus Infections
Shionogi · started 2025-12-11
📍 California · Florida · Georgia · Massachusetts · Missouri · New York · North Carolina · Ohio
NCT07214571 on ClinicalTrials.gov ↗
Recruiting
Phase 2
Recurrent Pericarditis, Heart Diseases, Pericarditis
Kiniksa Pharmaceuticals International, plc · started 2026-03-25
📍 Arizona · California · Florida · Illinois · Maryland · Minnesota · New York · Ohio
NCT07288216 on ClinicalTrials.gov ↗
Recruiting
Phase 2/Phase 3
Narcolepsy Type 1, Narcolepsy Type 2
Centessa Pharmaceuticals (UK) Limited · started 2026-05-29
📍 Colorado · Florida · Georgia · Mississippi · North Carolina · Ohio · South Carolina · Texas
NCT07598708 on ClinicalTrials.gov ↗
Active
Phase 3
Cholestatic Liver Disease (Except ALGS, PFIC, PBC and PSC)
Mirum Pharmaceuticals, Inc. · started 2024-10-14
📍 California · Illinois · New York · Ohio · Texas · Utah
NCT06553768 on ClinicalTrials.gov ↗
Recruiting
Phase 1/Phase 2
Synovial Sarcoma, Malignant Peripheral Nerve Sheath Tumor (MPNST), Neuroblastoma (NBL), Osteosarcoma
USWM CT, LLC · started 2023-09-01
📍 California · Maryland · Massachusetts · Missouri · New York · North Carolina · Ohio · Pennsylvania
NCT05642455 on ClinicalTrials.gov ↗
Recruiting
In-stent Thrombosis
Inari Medical · started 2024-09-09
📍 Connecticut · District of Columbia · Idaho · Maryland · New York · North Carolina · Ohio · Pennsylvania
NCT06394739 on ClinicalTrials.gov ↗
Recruiting
Phase 3
EPP, XLP
Tanabe Pharma America, Inc. · started 2021-08-10
📍 California · Florida · Massachusetts · Michigan · Missouri · New York · North Carolina · Ohio
NCT05005975 on ClinicalTrials.gov ↗
Active
Phase 2
Obesity, Overweight, Overweight With One Weight Related Comorbidity
Hoffmann-La Roche · started 2025-05-05
📍 Alabama · California · Florida · Georgia · Illinois · New York · North Carolina · Ohio
NCT06965413 on ClinicalTrials.gov ↗
Recruiting
Phase 1/Phase 2
Advanced Solid Tumors, Genital Neoplasm, Female, Urogenital Neoplasms, Lung Neoplasm
Marengo Therapeutics, Inc. · started 2023-01-04
📍 California · Florida · Kansas · Maryland · Massachusetts · Michigan · Ohio · Tennessee
NCT05592626 on ClinicalTrials.gov ↗
Active
Phase 1/Phase 2
Duchenne Muscular Dystrophy (DMD)
Dyne Therapeutics · started 2022-08-12
📍 California · Colorado · Georgia · Massachusetts · Ohio · Oregon · Pennsylvania · Utah
NCT05524883 on ClinicalTrials.gov ↗
Active
Phase 3
Influenza
ModernaTX, Inc. · started 2026-03-23
📍 California · Georgia · Idaho · Maryland · Nebraska · Ohio · Rhode Island · South Carolina
NCT07496450 on ClinicalTrials.gov ↗
Recruiting
Phase 2
Pulmonary Arterial Hypertension (PAH), Pulmonary Hypertension, Interstitial Lung Disease
AllRock Bio, Inc. · started 2025-10-01
📍 Arizona · California · Colorado · District of Columbia · Florida · Kansas · Michigan · Ohio
NCT07175038 on ClinicalTrials.gov ↗
Recruiting
Phase 1
Advanced Solid Tumor, Mesothelioma, Malignant
SpringWorks Therapeutics, Inc., a healthcare company of Merck KGaA, Darmstadt, Germany · started 2024-07-31
📍 Arizona · California · Ohio · Oregon · Texas
NCT06251310 on ClinicalTrials.gov ↗
Active
Phase 3
Generalized Anxiety Disorder
Definium Therapeutics US, Inc. · started 2025-01-29
📍 Arkansas · California · Florida · Georgia · Maryland · Massachusetts · New Jersey · Ohio
NCT06809595 on ClinicalTrials.gov ↗
Recruiting
Phase 2/Phase 3
Cancer-associated Cachexia
CatalYm GmbH · started 2026-04-16
📍 Connecticut · Florida · Georgia · New Jersey · Ohio
NCT07112196 on ClinicalTrials.gov ↗
Recruiting
Phase 3
Primary Membranous Nephropathy
Biogen · started 2025-05-22
📍 Alabama · California · Michigan · New York · North Carolina · Ohio · Tennessee · Texas
NCT06962800 on ClinicalTrials.gov ↗
Recruiting
Phase 1/Phase 2
Low Risk Myelodysplastic Syndromes
Rigel Pharmaceuticals · started 2022-09-12
📍 California · Florida · Missouri · New Jersey · New York · North Carolina · Ohio · Texas
NCT05308264 on ClinicalTrials.gov ↗
Recruiting
Phase 2/Phase 3
Fabry Disease
Chiesi Farmaceutici S.p.A. · started 2025-07-29
📍 Arizona · Georgia · Iowa · Ohio · Utah · Virginia
NCT06328608 on ClinicalTrials.gov ↗
Active
Phase 1
Ectonucleotide Pyrophosphatase/phosphodiesterase1 Deficiency, Autosomal Recessive Hypophosphatemic Rickets, Generalized Arterial Calcification of Infancy, ATP-Binding Cassette Subfamily C Member 6 Deficiency
Inozyme Pharma · started 2023-06-25
📍 California · Ohio · Pennsylvania
NCT05734196 on ClinicalTrials.gov ↗
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